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Amyloid transthyretin cardiomyopathy (ATTR-CM) is a progressive and life-threatening heart disease that can lead to increased ventricular wall thickness, restrictive cardiomyopathy, and heart failure.
A risk of pregnancy complications and adverse birth outcomes has been observed in mothers with alpha-1 antitrypsin deficiency (AATD), according to a study recently published in Plos One. The ...
Which of the statements below about the complications of immunoglobulin G4-related disease (IgG4-RD) are correct? Select one of the options for each question, then submit your answers to see how well ...
Patients with alpha-1 antitrypsin deficiency (AATD) receiving inhaled ATT therapy have demonstrated significant improvements in restoring protease–antiprotease homeostasis, according to results of a ...
A patient with chronic lymphocytic leukemia (CLL) achieved complete response after beginning methionine restriction (MR) in combination with chemotherapy. This case report was published in Cancer ...
A recent retrospective study highlighted the importance of human leukocyte antigen (HLA)-matched platelet units in improving outcomes for patients with immunized platelet transfusion refractoriness.
The CSHA Clinical Frailty Scale (CFS) is a valuable tool for predicting treatment-related toxicity and discontinuation in older adults receiving targeted therapy for chronic lymphocytic leukemia (CLL) ...
The administration of ARGX-119 led to improved survival and muscle function in a passive transfer myasthenia gravis (MG) mice model; however, the efficacy appears to be limited to a subset of patients ...
A strong association has been observed among patients with systemic mastocytosis (SM) who harbor the somatic missense KIT p.D816V variant in peripheral blood leukocytes and severe sting anaphylaxis. A ...
A male patient initially suspected of having immunoglobulin G4-related disease (IgG4-RD) had his diagnosis revised to Castleman disease following further investigations. This case report was published ...
Diffuse large B-cell lymphoma (DLBCL) is a type of cancer that originates in and affects the lymphatic system. 1 It is the most common type of non-Hodgkin lymphoma (NHL), accounting for approximately ...
Treatment with risdiplam over 30 months led to overall clinically meaningful improvement in most adult patients with spinal muscular atrophy (SMA) type 2 or 3, according to a single-center ...