Discover Sanfilippo Syndrome a rare genetic disorder affecting childrens development Learn about its symptoms treatment ...

Pharmaceutical announced new data demonstrating treatment with UX111 AAV gene therapy led to a statistically significant ...

NOVATO, Calif. - Ultragenyx Pharmaceutical Inc. (NASDAQ: NASDAQ:RARE), a $4.08 billion market cap biotechnology company with 27% revenue growth in the past year, today unveiled new data indicating ...

Tierney LaSotta was diagnosed with Sanfilippo Syndrome, a rare condition also known as Childhood Dementia because of its ...

An Orange couple who lost their son to a rare genetic condition are determined to continue raising awareness to improve the ...

The Grand Rapids Police Department will face the Kentwood Police Department in just one of the matchups scheduled for the ...

The daughter of a Kent County sheriff’s deputy who is fighting a rare genetic disorder will benefit from this year’s Robert ...

GRAND RAPIDS, MI -- The annual Robert Kozminski Memorial Basketball Game is Saturday, Feb. 1 and will benefit the young ...

The daughter of a Michigan sheriff’s deputy who is fighting a rare genetic disorder will benefit from the department’s annual charity event called the Robert Kozminski Memorial Basketball Games. The ...

This past December, Clark was diagnosed with Sanfilippo Syndrome. A neurological disease that causes Alzheimer-like symptoms in children. Clark’s parents say this surprise means everything to ...