As CRISPR and other gene editing therapies move into clinical trials, an important question remains—are these potentially life-saving treatments safe? Genome editing therapies hold great promise for ...

A new CRISPR breakthrough shows scientists can turn genes back on without cutting DNA, by removing chemical tags that act ...

This story is free to read because readers choose to support LAist. If you find value in independent local reporting, make a donation to power our newsroom today. Victoria Gray was wandering through ...

Beam Therapeutics set out to show how the precision of base-editing could produce new genetic medicines addressing a wide range of diseases. That goal may yet be realized, but the company is now ...

To continue reading this content, please enable JavaScript in your browser settings and refresh this page. Ryan Dodson, 18, was diagnosed with sickle cell disease ...

Base editors, DNA double-strand break (DSB)-independent genome modification agents, have been recognized alongside prime editors as key technologies to watch this year, 1 and advances to date have ...

Beam Therapeutics’ experimental gene-editing therapy for sickle cell disease now has its first cut of patient data showing signs of treating the rare blood disorder in a way that could differentiate ...

Sickle cell disease (SCD) is a group of blood disorders, including sickle cell anaemia, that is caused by stem blood cells producing mutated red blood cells. This leads to health complications, as the ...

Early tests show stem cells can be used to spark expression of a miniature version of the dystrophin protein. The combination of gene editing and patient-specific stem cells may offer a new ray of ...

At age 45, Dr. Lakiea Bailey said, for the longest time, that she was the oldest person with sickle cell anemia that she knew. The executive director of the nonprofit patient advocacy group the Sickle ...