For nearly three decades, Mayo Clinic researcher Christopher Evans, Ph.D., has pushed to expand gene therapy beyond its original scope of fixing rare, single-gene defects. That has meant ...
The gene therapy landscape has changed dramatically in the past 5 years, and investigators wanted to capture and analyze the details of current and upcoming trials, along with their potential impact ...
Conclusions These long-term findings in a large patient cohort show the sustained clinical efficacy and safety of autologous CD34+ hematopoietic stem-cell lentiviral gene therapy for ADA-SCID, ...
CHARLESTON, S.C. (WCSC) - You may have heard a friend say they’re “so OCD” or call an ex a “narcissist”, but mental health professionals say those words carry more weight than most people realize. The ...
December 26, 2025 A newly released clinical review is drawing attention within medical and regulatory communities by consolidating available evidence on the side-effect profile of a widely prescribed ...
A study published in the Journal of Clinical Oncology confirms that one of the first Food and Drug Administration-approved CAR-T cell therapies offers long-term survival and potential cures for adult ...
Nirogacestat therapy shows sustained benefits, including tumor shrinkage and durable responses, in long-term treatment of ...
MSK is the first hospital in New York City to offer gene therapy through its pediatric cancer program MSK Kids. Exagamglogene autotemcel (exa-cel) (Casgevy®) is a gene therapy for treating sickle cell ...
X-linked retinoschisis gene replacement therapy, aiming to improve retinal architecture and visual function in young male ...
The immune system is made up of different types of cells, which have different roles in protecting the body from infection. One type of immune cell called a B cell creates antibodies that attack ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results
Feedback