University of Iowa researchers successfully tested a nano-sized packet that released a single gene in newborn mice to prevent ...

University of Iowa researchers have successfully tested a gene-treatment technique to prevent craniosynostosis, a condition ...

Texas Children's is pleased to announce that a three-year-old girl has been successfully treated with the first-ever ...

University of Iowa researchers have successfully tested a gene-treatment technique to prevent craniosynostosis, a condition ...

A phase 3 trial highlights betibeglogene autotemcel as a potentially curative gene therapy for severe transfusion-dependent β-thalassemia.

Health systems must prepare for the growing impact of cell and gene therapies by addressing their high costs, complex care ...

Regeneron’s investigational gene therapy has been tied to notable hearing improvements in 10 of 11 children who were treated for a rare genetic condition that causes hearing loss.

For years, Stephanie McCabe and Andre Doucette accepted that their six-year-old son Emmett would die young. Now a possible ...

Gene therapy achieved its first major breakthroughs in the early 1990s with the treatment of a rare disease called severe combined immunodeficiency. However, the field was dealt a serious setback ...