An expert discusses how gene therapy represents a breakthrough treatment approach for BCG-unresponsive patients, offering ...

U.S. and China regulators have now cleared Sineugene Therapeutics' ALS gene therapy SNUG01 for clinical trials.

Sarepta is facing a number of issues currently, including platform-level safety concerns, management credibility issues, etc.

Gene therapy biotech Kriya Therapeutics has secured $313 million in a new series fundraise. | Gene therapy biotech Kriya ...

With approval to proceed, the Phase II trial (NCT06092034) of RP-A501 for Danon disease restarts under an optimized dosing ...

Ryuji Morizane, MD, Ph.D., of the Department of Medicine at Massachusetts General Hospital, is the senior/corresponding ...

Gene Therapy Trial Can Restart After Patient Death, FDA Says. The Sector Remains Depressed. The biotech Rocket ...

The FDA granted regenerative medicine advanced therapy designation to VG801 for the treatment of Stargardt disease, according to a press release from VeonGen Therapeutics. VG801, a dual-AAV gene ...

Genprex, Inc. ("Genprex" or the "Company") (NASDAQ: GNPX), a clinical-stage gene therapy company focused on developing ...

Jenny Craven, PharmD, BCPS, outlines the strategies UC Davis Health has used to successfully navigate the complex challenges ...

Children with spinal muscular atrophy (SMA) showed motor function improvements after switching to onasemnogene abeparvovec ...

Neovascular age-related macular degeneration (nAMD) is a progressive eye disease characterized by choroidal ...